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Value-Based Reimbursement Decisions for Orphan Drugs: A Scoping Review and Decision Framework
16 references·5 citing·38 second hop
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References

  • 2009Preferred reporting items for systematic reviews and meta-analyses: the PRISMA statement83,813 cited
  • 2009Preferred reporting items for systematic reviews and meta-analyses: the PRISMA Statement.44,857 cited
  • 2005Scoping studies: towards a methodological framework36,603 cited
  • 2002Qualitative data analysis for applied policy research4,965 cited
  • 2010Qualitative data analysis for applied policy research4,799 cited
  • 2002Analyzing Qualitative Data1,446 cited
  • 2008The NICE Cost-Effectiveness Threshold868 cited
  • 2001Synthesising research evidence.439 cited
  • 2002Evidence-based Policy: In Search of a Method403 cited
  • 2007Assessing the economic challenges posed by orphan drugs279 cited
  • 2011Pricing and reimbursement of orphan drugs: the need for more transparency261 cited
  • 2012The High Cost of Cancer Drugs and What We Can Do About It255 cited
  • 2011Characteristics of Clinical Trials to Support Approval of Orphan vs Nonorphan Drugs for Cancer230 cited
  • 2008Value based pricing for NHS drugs: an opportunity not to be missed?230 cited
  • 2005Orphan drugs and the NHS: should we value rarity?229 cited

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  • 2005Drugs for exceptionally rare diseases: do they deserve special status for funding?220 cited
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    • 2017HTA programme response to the challenges of dealing with orphan medicinal products: Process evaluation in selected European countries83 cited
    • 2016Why do health technology assessment coverage recommendations for the same drugs differ across settings? Applying a mixed methods framework to systematically compare orphan drug decisions in four European countries82 cited
    • 2017DRUG EVALUATION AND DECISION MAKING IN CATALONIA: DEVELOPMENT AND VALIDATION OF A METHODOLOGICAL FRAMEWORK BASED ON MULTI-CRITERIA DECISION ANALYSIS (MCDA) FOR ORPHAN DRUGS82 cited
    • 2015Can the EVIDEM Framework Tackle Issues Raised by Evaluating Treatments for Rare Diseases: Analysis of Issues and Policies, and Context-Specific Adaptation77 cited
    • 2018Multi-Criteria Decision Analysis (MCDA) Models in Health Technology Assessment of Orphan Drugs—a Systematic Literature Review. Next Steps in Methodology Development?76 cited